| Active substance | tofersen |
| Holder | Clinigen Healthcare Limited on behalf of Biogen |
| Status | Running |
| Indication | Amyotrophic Lateral Sclerosis (ALS) Associated with a Mutation in the Superoxide Dismutase 1 (SOD1) Gene |
| Public documents | Approbation |
| Information for the patient | |
| Informed consent | |
| Last update | 18/04/2024 |