Active substance | Elexacaftor/Tezacaftor/Ivacaftor and Ivacaftor |
Holder | Parexel International on behalf of Vertex Pharmaceuticals Incorporated |
Status | closed |
Indication | for Patients 2 Through 5 Years of Age With Cystic Fibrosis Who Have At Least One F508del Mutation in the Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) Gene |
Public documents | Approbation |
Information for the patient | |
Informed consent | |
Last update | 29/11/2024 |